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Scientific distinctions between coca and cocaine support policy reform

1 month 2 weeks ago
Science, Volume 390, Issue 6775, Page 782-785, November 2025.
Dawson M. White, Ricardo Soberón Garrido, Caroline S. Conzelman, Wade Davis, Claude Guislain, Anthony Henman, Orlando Adolfo Jara-Muñoz, Martin Jelsma, Susana Mejía, Daniel Montoya-Cataño, Oscar Alejandro Pérez-Escobar, David Alfonso Restrepo, Yenny…

Phase 1/2a clinical trial of hESC-derived dopamine progenitors in Parkinson's disease

1 month 3 weeks ago
Parkinson's disease (PD) has long been considered an appropriate candidate for cell replacement therapy. We generated high-purity dopaminergic progenitors (A9-DPCs) from human embryonic stem cells and evaluated their safety and exploratory efficacy in a single-center, open-label, dose-escalation phase 1/2a trial (NCT05887466) for PD patients. Twelve patients with moderate-to-severe PD received bilateral putamen transplantation of low-dose (3.15 million cells; n = 6) or high-dose (6.30 million...
Jin Woo Chang

Beyond Krabbe disease, the intriguing connection of galactocerebrosidase (GALC) with nervous system illness: A novel risk factor?

1 month 3 weeks ago
Galactocerebrosidase (GALC) is a lysosomal enzyme crucially involved in the catabolism of galactosphingolipids. Among galactosphingolipids, galactosylceramide and sulfatide are crucial determinants for oligodendrocyte differentiation, as well as myelin stability and structure. Homozygous or compound heterozygous inherited mutations leading to a severe decrease in GALC enzymatic activity have been associated with the onset of Krabbe disease, also known as "globoid cell leukodystrophy". Extensive...
Nadia Papini